By the same authors

From the same journal

Orphan drugs revisited: [comment]

Research output: Contribution to journalArticlepeer-review



Publication details

JournalQJM Monthly Journal of the Association of Physicians
DatePublished - May 2006
Issue number5
Pages (from-to)341-5
Original languageEnglish


Hughes et al.1 recently discussed arguments for and against giving special funding status to orphan drugs in this journal. They concluded that there should be a uniform policy across Europe, that complete restriction was impractical, and that UK policy should aspire to the values of the EU directive. The aims of this paper are to correct some inaccuracies in the original paper, develop some of the key issues, and to draw some conclusions regarding the question ‘Do drugs for exceptionally rare disease deserve special status for funding?’ For ease, our paper adopts the same structure as the original.

Bibliographical note

© The Author 2006. Published by Oxford University Press on behalf of the Association of Physicians. All rights reserved. For Permissions, please email: The online version of this article has been published under an open access model. Users are entitled to use, reproduce, disseminate, or display the open access version of this article for non-commercial purposes provided that: the original authorship is properly and fully attributed; the Journal and Oxford University Press are attributed as the original place of publication with the correct citation details given; if an article is subsequently reproduced or disseminated not in its entirety but only in part or as a derivative work this must be clearly indicated. For commercial re-use, please contact

    Research areas

  • Attitude of Health PersonnelEthics, MedicalEuropeHumansLegislation, Drug/es [Ethics]*Orphan Drug Production/ec [Economics]Orphan Drug Production/es [Ethics]Orphan Drug Production/lj [Legislation & Jurisprudence]*Rare Diseases/dt [Drug Therapy]Rare Diseases/ec [Economics], RARE DISEASES

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